
Therapeutics Program
Delivering fundamental cures for intractable diseases through CRISPR-Cas9 gene-editing therapeutics.

Red Bio: Therapy
Red Bio leverages our foundational CRISPR-Cas9 technology to develop ‘Genomic cures’ targeting disease root causes. We address unmet medical needs through In Vivo platforms offering long-term efficacy from a single dose, and enhanced Ex Vivo cell therapies.
Advancing a robust pipeline, we deliver fundamental treatments to solve humanity’s greatest challenges: innovating medicines and extending life.

In Vivo
In Vivo gene therapy delivers editing agents directly to patients to correct disease-causing genes in target organs. This approach effectively addresses systemic diseases and organs that are difficult to culture. It offers long-term efficacy from a single dose by targeting the root cause.
Leveraging this powerful technology, we are advancing a robust pipeline of innovative therapeutics. Our paradigm-shifting treatments overcome conventional limits, advancing human health and extending life.

Ex Vivo
Ex Vivo gene editing maximizes safety by precisely modifying patient or donor cells outside the body before reinfusion. By combining living cell technologies with advanced gene editing techniques, we can deliver highly optimized, customized treatments for immune and rare diseases with maximum efficacy.
Using this platform, we are developing next-generation cell therapies to address unmet medical needs and provide safe, innovative options for treating intractable diseases.
In Vivo
| Program (Disease) | Modeling | in vitro | in vivo | POC | IND-enabling | IND | Phase 1 | Partner |
|---|---|---|---|---|---|---|---|---|
GEB-200 | CRISPR-Based Lp(a) Suppression Cardiovascular | ![]() | |||||||
TGT-202 | Liver Biofactory Platform, LBP Liver | ||||||||
TGT-201 | Hemophilia A & B (Including Inhibitors) Liver | ||||||||
Ex Vivo
| Program (Disease) | Modeling | in vitro | in vivo | POC | IND-enabling | IND | Phase 1 | Partner |
|---|---|---|---|---|---|---|---|---|
Styx-T Platform-1 | Next-Generation CAR-T Immune cell | ![]() | |||||||
4th Armored CAR-T Solid Tumor | ||||||||
iPSC Platform | ||||||||




























