ToolGen

Therapeutics Program

Delivering fundamental cures for intractable diseases through CRISPR-Cas9 gene-editing therapeutics.

Red Bio: Therapy

Red Bio: Therapy

Red Bio leverages our foundational CRISPR-Cas9 technology to develop ‘Genomic cures’ targeting disease root causes. We address unmet medical needs through In Vivo platforms offering long-term efficacy from a single dose, and enhanced Ex Vivo cell therapies.
Advancing a robust pipeline, we deliver fundamental treatments to solve humanity’s greatest challenges: innovating medicines and extending life.

In Vivo

In Vivo

In Vivo gene therapy delivers editing agents directly to patients to correct disease-causing genes in target organs. This approach effectively addresses systemic diseases and organs that are difficult to culture. It offers long-term efficacy from a single dose by targeting the root cause.
Leveraging this powerful technology, we are advancing a robust pipeline of innovative therapeutics. Our paradigm-shifting treatments overcome conventional limits, advancing human health and extending life.

Ex Vivo

Ex Vivo

Ex Vivo gene editing maximizes safety by precisely modifying patient or donor cells outside the body before reinfusion. By combining living cell technologies with advanced gene editing techniques, we can deliver highly optimized, customized treatments for immune and rare diseases with maximum efficacy.
Using this platform, we are developing next-generation cell therapies to address unmet medical needs and provide safe, innovative options for treating intractable diseases.

In Vivo

Program (Disease)Modelingin vitroin vivoPOCIND-enablingINDPhase 1Partner
GEB-200 | CRISPR-Based Lp(a) Suppression
Cardiovascular
GenEditBio
TGT-202 | Liver Biofactory Platform, LBP
Liver
TGT-201 | Hemophilia A & B (Including Inhibitors)
Liver

Ex Vivo

Program (Disease)Modelingin vitroin vivoPOCIND-enablingINDPhase 1Partner
Styx-T Platform-1 | Next-Generation CAR-T
Immune cell
Cartherics
4th Armored CAR-T
Solid Tumor
iPSC Platform

Partnered with

  • 티앤알바이오팹
  • GenEditBio
  • Cartherics
  • Ministry of Trade, Industry and Energy
  • KeyGene NV.
  • Thermo Fisher Scientific
  • ㈜옵티팜
  • ㈜오리엔트바이오
  • ㈜엠케이바이오텍
  • ㈜바이오앱
  • ㈜엔세이지
  • 지에이치바이오㈜
  • 엔비엠㈜
  • ㈜바이오니아
  • ㈜에스엘바이젠
  • ㈜라트바이오
  • ㈜젬크로
  • ㈜바이오에프디엔씨
  • ㈜눌라바이오
  • Bioseed Research
  • 오가노이드사이언스㈜
  • ㈜아비노젠
  • IBS 기초과학연구원
  • 몬산토
  • 바이엘 퓨리
  • 삼성서울병원
  • 충남대학교 산학협력단
  • 농우바이오
  • 플랜트아크바이오
  • DNAharvest